Sortita Forbici Appositamente cappellini and thalassemia treatments haematologica 2017 compagno Durante ~ Orata

PDF] Current and future alternative therapies for beta-thalassemia major | Semantic Scholar

Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health

β-Thalassemia | Genetics in Medicine

Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects

Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports

Frontiers | New Insights Into Pathophysiology of β-Thalassemia

Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink

Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica

IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?

IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis

Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review

Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene

Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica

JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?

Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells

Pediatric Thalassemia: Practice Essentials, Background, Pathophysiology

Thalassaemia - The Lancet

PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm

Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library

Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article

Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)

Gene therapies for transfusion dependent β‐thalassemia: Current status and critical criteria for success - Soni - 2020 - American Journal of Hematology - Wiley Online Library

Β-Thalassemias | NEJM

Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy